A novel gene therapy approach has given five children who were born deaf the ability to hear. The method, which overcomes a roadblock presented by large genes, may be useful in other treatments, according to researchers.

Boston Children's Hospital Answers article on new research from from the teams of Maria Lehtinen, Mark Andermann, Hanno Steen, and clinician colleagues at Boston Children’s Hospital and Mass General Hospital, co-first authors Cameron Sadegh and Huixin Xu, suggesting that gene therapy targeting the brain’s choroid plexus could help prevent or ameliorate hydrocephalus in premature newborns with brain bleeds.