Neuro Topics - Gene editing
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May 9, 2024
Results from a small proof-of-concept study indicate that CRISPR gene editing is safe and can improve vision in some people with inherited blindness. In the multicenter clinical trial, 11 of the 14 individuals treated had measurable improvements on at least one key vision test, while six people experienced improvement on two or more vision outcomes.
Original article in: New England Journal of Medicine >
July 3, 2019
HMS News article on new research from the labs of David Corey, Jeffrey Holt and Gwenaëlle Géléoc. They used a newly optimized gene-editing tool to prevent hearing loss in mice with hereditary deafness without detectable off-target effects.
Original article in: Nature Medicine >